Category of Chemicals

CFTR regulators are a class of medications designed to treat cystic fibrosis (CF), a genetic disease causing thick and sticky mucus in the respiratory and digestive systems. Unlike CFTR inhibitors, regulators aim to enhance the function of defective CFTR proteins. By promoting proper chloride ion transport, CFTR regulators help thin mucus, improve lung function, and alleviate symptoms. This innovative approach provides much-needed relief for CF patients and represents a significant advancement in CF therapy.